C11ORF65

Chr 11

chromosome 11 open reading frame 65

Also known as: MFI

The protein acts as an inhibitor of mitochondrial fission by interacting with MFF and preventing DNM1L recruitment to mitochondria, promoting mitochondrial fusion. Mutations cause autosomal recessive spastic paraplegia-76, which presents with progressive spasticity primarily affecting the lower limbs. This gene shows tolerance to loss-of-function variants based on constraint metrics.

ResearchSummary from RefSeq, UniProt
LOEUF 1.75
Clinical SummaryC11ORF65
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
101 unique Pathogenic / Likely Pathogenic· 203 VUS of 400 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.75LOEUF
pLI 0.000
Z-score -0.80
OE 1.22 (0.851.75)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
0.37Z-score
OE missense 0.92 (0.801.05)
148 obs / 161.2 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE1.22 (0.851.75)
00.351.4
Missense OE0.92 (0.801.05)
00.61.4
Synonymous OE0.84
01.21.6
LoF obs/exp: 19 / 15.6Missense obs/exp: 148 / 161.2Syn Z: 0.90

ClinVar Variant Classifications

400 submitted variants in ClinVar

Classification Summary

Pathogenic75
Likely Pathogenic26
VUS203
Likely Benign68
Benign3
75
Pathogenic
26
Likely Pathogenic
203
VUS
68
Likely Benign
3
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
73
0
2
0
75
Likely Pathogenic
22
3
1
0
26
VUS
3
162
32
6
203
Likely Benign
0
6
39
23
68
Benign
0
0
3
0
3
Total981717729375

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

C11ORF65 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found