C10ORF126

Chr 10

chromosome 10 open reading frame 126

Also known as: bA492M23.1

The protein is involved in mitochondrial ribosome assembly and function. Biallelic mutations cause severe early-onset mitochondrial disease with developmental delay, hypotonia, and metabolic acidosis. This gene follows autosomal recessive inheritance and shows low constraint against loss-of-function variants.

0
Active trials
0
Pubs (1 yr)
14
P/LP submissions
P/LP missense
1.81
LOEUF
Mechanism
Clinical SummaryC10ORF126
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
14 unique Pathogenic / Likely Pathogenic· 1 VUS of 21 total submissions
Some data sources returned errors (1)

ensembl: Error: Ensembl fetch failed: 400 for https://rest.ensembl.org/lookup/symbol/homo_sapiens/C10ORF126?content-type=application/json&expand=1

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.81LOEUF
pLI 0.002
Z-score 0.10
OE 0.95 (0.461.81)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
0.90Z-score
OE missense 0.72 (0.590.90)
60 obs / 83.0 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.95 (0.461.81)
00.351.4
Missense OE0.72 (0.590.90)
00.61.4
Synonymous OE0.86
01.21.6
LoF obs/exp: 4 / 4.2Missense obs/exp: 60 / 83.0Syn Z: 0.61

ClinVar Variant Classifications

21 submitted variants in ClinVar

Classification Summary

Pathogenic13
Likely Pathogenic1
VUS1
Likely Benign1
Benign1
13
Pathogenic
1
Likely Pathogenic
1
VUS
1
Likely Benign
1
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories· variant type breakdown unavailable

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
13
Likely Pathogenic
1
VUS
1
Likely Benign
1
Benign
1
Total17

Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

C10ORF126 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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