BCKDK

Chr 16AR

branched chain keto acid dehydrogenase kinase

The protein phosphorylates and inactivates the branched-chain alpha-ketoacid dehydrogenase complex in the mitochondrial matrix, regulating the catabolism of valine, leucine, and isoleucine. Mutations cause branched-chain keto acid dehydrogenase kinase deficiency through an autosomal recessive inheritance pattern. The pathogenic mechanism involves dominant-negative effects.

OMIMResearchSummary from RefSeq, OMIM, UniProt, Mechanism
MultiplemechanismARLOEUF 0.871 OMIM phenotype
Clinical SummaryBCKDK
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Gene-Disease Validity (ClinGen)
branched-chain keto acid dehydrogenase kinase deficiency · ARDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
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Clinical Trials
1 active or recruiting trial — potential therapeutic options may be available
Some data sources returned errors (1)

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Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.87LOEUF
pLI 0.000
Z-score 2.00
OE 0.51 (0.310.87)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
1.64Z-score
OE missense 0.73 (0.650.82)
209 obs / 287.1 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.51 (0.310.87)
00.351.4
Missense OE0.73 (0.650.82)
00.61.4
Synonymous OE1.02
01.21.6
LoF obs/exp: 10 / 19.6Missense obs/exp: 209 / 287.1Syn Z: -0.18
DN
0.7325th %ile
GOF
0.6638th %ile
LOF
0.2872th %ile

This gene has evidence for multiple mechanisms of pathogenicity (dominant-negative and gain-of-function). Both the Badonyi & Marsh prediction and the broader genomic evidence point to dominant-negative as the predominant mechanism. Different variants in this gene may act through different mechanisms — interpret in context of the specific variant.

DNprediction above median
GOFprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

BCKDK · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
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