B3GALNT2

Chr 1AR

beta-1,3-N-acetylgalactosaminyltransferase 2

Also known as: B3GalNAc-T2, MDDGA11

The protein is a beta-1,3-N-acetylgalactosaminyltransferase that synthesizes a unique carbohydrate structure on N- and O-glycans and is specifically involved in alpha-dystroglycan glycosylation, which is required for binding laminin and other extracellular proteins. Biallelic mutations cause congenital muscular dystrophy-dystroglycanopathy type A11, characterized by congenital onset muscular dystrophy with brain and eye anomalies. This condition follows autosomal recessive inheritance.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismARLOEUF 0.841 OMIM phenotype
Clinical SummaryB3GALNT2
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Gene-Disease Validity (ClinGen)
muscular dystrophy-dystroglycanopathy (congenital with brain and eye anomalies), type a, 11 · ARDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
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Clinical Trials
1 active or recruiting trial — potential therapeutic options may be available

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.84LOEUF
pLI 0.000
Z-score 2.20
OE 0.55 (0.360.84)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
0.95Z-score
OE missense 0.84 (0.750.93)
222 obs / 265.6 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.55 (0.360.84)
00.351.4
Missense OE0.84 (0.750.93)
00.61.4
Synonymous OE0.91
01.21.6
LoF obs/exp: 15 / 27.4Missense obs/exp: 222 / 265.6Syn Z: 0.72
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
definitiveB3GALNT2-related muscular dystrophy-dystroglycanopathy (congenital with brain and eye anomalies), type ALOFAR

Predictions shown for reference only — model trained on dominant genes, not applicable to AR conditions.

DN
0.6355th %ile
GOF
0.6735th %ile
LOF
0.2678th %ile

The Badonyi & Marsh prediction model was trained exclusively on dominant disease genes. Predictions are not reliable for genes with autosomal recessive inheritance and are shown at reduced opacity for reference only.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

B3GALNT2 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC