AZIN1

Chr 8

antizyme inhibitor 1

Also known as: AZI, AZI1, AZIA1, OAZI, OAZIN, ODC1L

This antizyme inhibitor protein positively regulates ornithine decarboxylase activity and polyamine uptake by sequestering antizymes and preventing ornithine decarboxylase degradation, which is essential for maintaining cellular polyamine homeostasis required for growth and proliferation. Mutations cause autosomal recessive developmental abnormalities with perinatal lethality and liver morphological defects. The gene is highly constrained against loss-of-function variants, consistent with its essential role in early development.

Summary from RefSeq, UniProt
Research Assistant →
0
Active trials
8
Pubs (1 yr)
40
P/LP submissions
0%
P/LP missense
0.24
LOEUF· LoF intol.
Mechanism
Clinical SummaryAZIN1
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 0.99). One damaged copy is likely sufficient to cause disease.
📋
ClinVar Variants
40 unique Pathogenic / Likely Pathogenic· 37 VUS of 101 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

LoF intolerant — likely haploinsufficient
LoF Constraint
0.24LOEUF
pLI 0.995
Z-score 3.94
OE 0.05 (0.020.24)
Highly constrained

Highly LoF-intolerant (top ~10% of genes)

Missense Constraint
1.80Z-score
OE missense 0.67 (0.580.76)
155 obs / 232.4 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.05 (0.020.24)
00.351.4
Missense OE0.67 (0.580.76)
00.61.4
Synonymous OE1.00
01.21.6
LoF obs/exp: 1 / 20.0Missense obs/exp: 155 / 232.4Syn Z: -0.01

ClinVar Variant Classifications

101 submitted variants in ClinVar

Classification Summary

Pathogenic38
Likely Pathogenic2
VUS37
Likely Benign2
38
Pathogenic
2
Likely Pathogenic
37
VUS
2
Likely Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
38
0
38
Likely Pathogenic
0
0
2
0
2
VUS
0
33
4
0
37
Likely Benign
0
1
0
1
2
Benign
0
0
0
0
0
Total03444179

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

AZIN1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
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