ATP5F1C

Chr 10

ATP synthase F1 subunit gamma

Also known as: ATP5C, ATP5C1, ATP5CL1

The protein is the gamma subunit of mitochondrial ATP synthase (Complex V), which produces ATP from ADP using the proton gradient generated by the respiratory chain and is essential for F1 catalytic domain assembly. Mutations cause autosomal recessive mitochondrial complex V deficiency, presenting as a severe mitochondrial disorder affecting multiple organ systems. The gene shows low constraint to loss-of-function variants, consistent with autosomal recessive inheritance where heterozygous carriers are typically unaffected.

Summary from RefSeq, UniProt
Research Assistant →
0
Active trials
4
Pubs (1 yr)
25
P/LP submissions
0%
P/LP missense
0.81
LOEUF
DN
Mechanism· predicted
Clinical SummaryATP5F1C
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
25 unique Pathogenic / Likely Pathogenic· 44 VUS of 87 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.81LOEUF
pLI 0.001
Z-score 2.15
OE 0.45 (0.260.81)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
0.80Z-score
OE missense 0.82 (0.710.95)
134 obs / 162.7 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.45 (0.260.81)
00.351.4
Missense OE0.82 (0.710.95)
00.61.4
Synonymous OE0.77
01.21.6
LoF obs/exp: 8 / 17.8Missense obs/exp: 134 / 162.7Syn Z: 1.41
DN
0.7133th %ile
GOF
0.4184th %ile
LOF
0.3164th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

87 submitted variants in ClinVar

Classification Summary

Pathogenic24
Likely Pathogenic1
VUS44
Likely Benign2
Benign1
24
Pathogenic
1
Likely Pathogenic
44
VUS
2
Likely Benign
1
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
24
0
24
Likely Pathogenic
0
0
1
0
1
VUS
0
35
9
0
44
Likely Benign
0
2
0
0
2
Benign
0
0
1
0
1
Total03735072

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

ATP5F1C · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC