ARHGAP39

Chr 8

Rho GTPase activating protein 39

Also known as: CrGAP, Vilse

ARHGAP39 encodes a protein with GTPase activator activity that functions in postsynaptic organization at glutamatergic synapses. Mutations cause autosomal recessive neurodevelopmental disorders with intellectual disability and seizures. The gene shows high constraint against loss-of-function variants (LOEUF 0.45), consistent with its essential role in synaptic function.

Summary from RefSeq
Research Assistant →
0
Active trials
2
Pubs (1 yr)
56
P/LP submissions
0%
P/LP missense
0.45
LOEUF
DN
Mechanism· predicted
Clinical SummaryARHGAP39
Population Constraint (gnomAD)
Constrained for loss-of-function variants (OE-LoF 0.28) despite low pLI — interpret in context.
📋
ClinVar Variants
56 unique Pathogenic / Likely Pathogenic· 198 VUS of 297 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.45LOEUF
pLI 0.008
Z-score 4.51
OE 0.28 (0.180.45)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
2.52Z-score
OE missense 0.74 (0.690.79)
534 obs / 725.3 exp
Mild constraint

Moderately missense-constrained (top ~2.5%)

Observed / Expected Ratios
LoF OE0.28 (0.180.45)
00.351.4
Missense OE0.74 (0.690.79)
00.61.4
Synonymous OE1.07
01.21.6
LoF obs/exp: 13 / 46.0Missense obs/exp: 534 / 725.3Syn Z: -0.96
DN
0.6455th %ile
GOF
0.5856th %ile
LOF
0.3744th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

297 submitted variants in ClinVar

Classification Summary

Pathogenic51
Likely Pathogenic5
VUS198
Likely Benign14
Benign4
51
Pathogenic
5
Likely Pathogenic
198
VUS
14
Likely Benign
4
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
51
0
51
Likely Pathogenic
0
0
5
0
5
VUS
0
184
14
0
198
Likely Benign
0
9
2
3
14
Benign
0
0
2
2
4
Total0193745272

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

ARHGAP39 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC