APELA

Chr 4

apelin receptor early endogenous ligand

Also known as: ELA, Ende, tdl

This gene encodes a peptide hormone that binds to the Apelin receptor. The encoded protein is required for heart development in zebrafish and has been shown to maintain self-renewal of human embryonic stem cells through activation of the PI3K/AKT pathway. Experiments in human and mouse cell lines point to additional roles for the encoded protein in angiogenesis and regulation of vascular tone. [provided by RefSeq, Jul 2016]

OMIMResearchGenerating clinical summary…
12
Active trials
13
Pubs (1 yr)
P/LP submissions
P/LP missense
LOEUF
Multiple*
Mechanism· predicted

Population Genetics & Constraint

Constraint data not available from gnomAD.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

APELA · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

Muscular Atrophy, Spinal

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

RECRUITING
NCT05861999Phase PHASE4Hoffmann-La RocheStarted 2024-08-14
Risdiplam
CLN7

Study for the Treatment for CLN7 Disease

ACTIVE NOT RECRUITING
NCT04737460Phase PHASE1Benjamin GreenbergStarted 2021-05-04
AAV9/CLN7
Infant NeurodevelopmentNutritionMethylation

Maternal Methyl-Nutrient Status and Infant Neurodevelopment Study

RECRUITING
NCT07568561Far Eastern Memorial HospitalStarted 2026-05-27
Cerebral Palsy

CP-EDIT: Cerebral Palsy - Early Diagnosis and Intervention Trial

RECRUITING
NCT05835674Rigshospitalet, DenmarkStarted 2023-04-01
Early intervention program
Postnatal Depression

Home-based Transcranial Direct Current Stimulation in Postpartum Depression: the Feasibility Study and Pilot Study

NOT YET RECRUITING
NCT05046405Phase NAAna Ganho ÁvilaStarted 2022-10-02
Transcranial Direct Current Stimulation
HSPHereditary Spastic ParaplegiaHereditary Spastic Paraparesis

Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47)

NOT YET RECRUITING
NCT06948019Phase PHASE1, PHASE2BlackfinBio LtdStarted 2025-08
BFB-101 (AAV9-CBh-AP4B1)
MPS IIIASanfilippo SyndromeSanfilippo A

Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH

RECRUITING
NCT02716246Phase PHASE2, PHASE3Ultragenyx Pharmaceutical IncStarted 2016-04-25
UX111Prophylactic Immunomodulatory (IM) TherapyOptimized Prophylactic IM Therapy
NGLY1 Deficiency

Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency

ACTIVE NOT RECRUITING
NCT06199531Phase PHASE3Grace Science, LLCStarted 2024-02-13
GS-100
Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency DiseaseOrnithine Carbamoyltransferase Deficiency (Disorder)

An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency

RECRUITING
NCT06255782Phase PHASE3iECURE, Inc.Started 2024-04-08
ECUR-506
Muscular Atrophy, Spinal

A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy

ACTIVE NOT RECRUITING
NCT03779334Phase PHASE2Hoffmann-La RocheStarted 2019-08-07
Risdiplam
Gaucher Disease, Type 2

Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)

ACTIVE NOT RECRUITING
NCT04411654Phase PHASE1, PHASE2Prevail TherapeuticsStarted 2021-06-29
LY3884961MethylprednisoloneSirolimus
MPS IIHunter Syndrome (MPS II)

RGX-121-3102 Gene Therapy in Participants With MPS II (Hunter Syndrome)

ACTIVE NOT RECRUITING
NCT07236606Phase PHASE3REGENXBIO Inc.Started 2025-11-25
RGX-121-3102