ALG13

Chr XX-linked

ALG13 UDP-N-acetylglucosaminyltransferase subunit

Also known as: CDG1S, CXorf45, DEE36, EIEE36, GLT28D1, MDS031, TDRD13, YGL047W

The ALG13 protein is the catalytic subunit of a UDP-N-acetylglucosamine transferase complex that catalyzes the second step in dolichol-linked oligosaccharide biosynthesis, essential for N-linked protein glycosylation in the endoplasmic reticulum. Mutations cause developmental and epileptic encephalopathy 36 through an X-linked inheritance pattern, predominantly through loss-of-function mechanisms that disrupt this critical glycosylation pathway. The gene shows extreme intolerance to loss-of-function variants, consistent with haploinsufficiency being pathogenic in this X-linked disorder.

OMIMResearchSummary from RefSeq, OMIM, UniProt, Mechanism
LOFmechanismX-linkedLOEUF 0.161 OMIM phenotype
Clinical SummaryALG13
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Gene-Disease Validity (ClinGen)
developmental and epileptic encephalopathy · XLDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 1.00). One damaged copy is likely sufficient to cause disease.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

LoF intolerant — likely haploinsufficient
LoF Constraint
0.16LOEUF
pLI 1.000
Z-score 5.51
OE 0.05 (0.020.16)
Highly constrained

Highly LoF-intolerant (top ~10% of genes)

Missense Constraint
1.15Z-score
OE missense 0.84 (0.770.92)
332 obs / 396.3 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.05 (0.020.16)
00.351.4
Missense OE0.84 (0.770.92)
00.61.4
Synonymous OE1.08
01.21.6
LoF obs/exp: 2 / 39.2Missense obs/exp: 332 / 396.3Syn Z: -0.72
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
strongALG13-related congenital disorder of glycosylationOTHERmonoallelic_X_heterozygous
DN
0.2898th %ile
GOF
0.3491th %ile
LOF
0.78top 5%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · LOEUF 0.16

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

ALG13 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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Key Publications
Landmark & review papers · by relevance
PubMed
Top 5 results · since 2015Search PubMed ↗