ALDH7A1

Chr 5AR

aldehyde dehydrogenase 7 family member A1

Also known as: ATQ1, EPD, EPEO4, PDE

ALDH7A1 encodes an aldehyde dehydrogenase enzyme that metabolizes aldehydes from lipid peroxidation and alcohol metabolism, and converts betaine aldehyde to betaine for cellular osmotic protection. Mutations cause pyridoxine-dependent epilepsy with early onset, inherited in an autosomal recessive pattern. The gene is not constrained against loss-of-function variants, and patients typically respond to vitamin B6 supplementation.

GeneReviewsOMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismARLOEUF 1.241 OMIM phenotype
Clinical SummaryALDH7A1
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Gene-Disease Validity (ClinGen)
pyridoxine-dependent epilepsy · ARDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
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Clinical Trials
1 active or recruiting trial — potential therapeutic options may be available
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GeneReview available — ALDH7A1
Authoritative clinical overview · Recommended first read
Open GeneReview ↗

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.24LOEUF
pLI 0.000
Z-score 0.37
OE 0.93 (0.711.24)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
0.37Z-score
OE missense 0.94 (0.851.04)
278 obs / 295.8 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.93 (0.711.24)
00.351.4
Missense OE0.94 (0.851.04)
00.61.4
Synonymous OE1.02
01.21.6
LoF obs/exp: 35 / 37.4Missense obs/exp: 278 / 295.8Syn Z: -0.18
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
definitiveALDH7A1-related pyridoxine-dependent epilepsyLOFAR

Predictions shown for reference only — model trained on dominant genes, not applicable to AR conditions.

DN
0.6647th %ile
GOF
0.6345th %ile
LOF
0.4431th %ile

The Badonyi & Marsh prediction model was trained exclusively on dominant disease genes. Predictions are not reliable for genes with autosomal recessive inheritance and are shown at reduced opacity for reference only.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

ALDH7A1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
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