AGO3

Chr 1

argonaute RISC catalytic component 3

Also known as: EIF2C3

The protein is an Argonaute family member that binds small RNAs like microRNAs and mediates RNA interference by repressing translation of complementary mRNAs and degrading select target RNAs. Mutations cause neurodevelopmental disorders with intellectual disability, developmental delay, and behavioral abnormalities, inherited in an autosomal dominant pattern. This gene is highly constrained against loss-of-function variation, indicating that functional copies are essential for normal development.

OMIMResearchSummary from RefSeq, UniProt
LOEUF 0.19
Clinical SummaryAGO3
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 1.00). One damaged copy is likely sufficient to cause disease.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Dual constrained — LoF & missense intolerant
LoF Constraint
0.19LOEUF
pLI 1.000
Z-score 5.84
OE 0.08 (0.040.19)
Highly constrained

Highly LoF-intolerant (top ~10% of genes)

Missense Constraint
5.26Z-score
OE missense 0.34 (0.300.39)
170 obs / 501.4 exp
Constrained

Extremely missense-constrained (top ~0.01%)

Observed / Expected Ratios
LoF OE0.08 (0.040.19)
00.351.4
Missense OE0.34 (0.300.39)
00.61.4
Synonymous OE0.85
01.21.6
LoF obs/exp: 4 / 47.4Missense obs/exp: 170 / 501.4Syn Z: 1.55

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

AGO3 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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